Drug News Abstracts - September 2021


COVID Boosters Supported by CDC, Fauci

In a White House press briefing, U.S. health officials laid out the case for a scientific rationale for administering a third dose of the COVID-19 mRNA vaccines for all U.S. adults. CDC Director Rochelle Walensky presented evidence that showed that vaccine effectiveness has been decreasing over time against both symptomatic and asymptomatic infections, although protection against severe disease, hospitalizations, and death remains relatively high. Dr. Walensky presented evidence from several studies published in MMWR and by the Mayo Clinic (posted on medRxiv).

READ MORE...

Triple-Drug Therapy Effective for Cystic Fibrosis

Use of a three-drug combination improved lung functionand sweatchloride concentration relative to an active control in a subclass of patients with cystic fibrosis.In a phase 3, double-blind, randomized, active-control trial, the three-drug combination ivacaftor–tezacaftor–elexacaftor was tested as treatment for cystic fibrosis in patients who had Phe508del-gating or Phe508del-residual function genotypes. In cystic fibrosis, deficiencies in the cystic fibrosis transmembrane conductance regulator (CFTR) proteins manifests in progressive respiratory impairment, exocrine pancreatic insufficiency, hepatobiliary disease, and abnormal sweat composition. Cystic fibrosis results from biallelic mutations in the CFTR gene, among them processing mutations, which reduce the quantity of CFTR protein on the cell surface; channel-gating defects, which limit anion transport; and residual function mutations, which result in lesser impairment of CFTR protein activity. Ivacaftor is a CFTR potentiator that augments gating of mutant CFTR proteins, tezacaftor is a CFTR corrector that acts to ease the defects of CFTR processing and cell-surface trafficking intrinsic to Phe508del, andelexacaftor is a CFTR corrector with a mechanism of action complementary to tezacaftor.

READ MORE...

Atopegant: An Effective Oral Migraine Preventive

Once-daily oral treatment with atopegant, a small-molecule, calcitonin gene-related peptide (CGRP) receptor antagonist, was effective in reducing the number of migraine days and headache days over 12 weeks in patients with episodic migraine. These are the findings of ADVANCE, a phase 3multinational, randomized, double-blind, parallel-group, placebo-controlled trial that examined three dosage strengths of atopegant for prevention of migraine.

READ MORE...